Development of a New Medication for the Ultra-Rare Mitochondrial Disease Thymidine Kinase 2 Deficiency Disorder (TK2d)

Time: 2:30 pm
day: Day Two

Details:

  • Reviewing TK2d disease whilst navigating natural history
  • Evaluating the creation of NDA-supporting dataset
  • Examining top-line results supporting NDA-submission

Speakers: